1. A Bayesian comparative effectiveness trial in action: developing a platform for multisite study adaptive randomization. Issue 1 (December 2016) Authors: Brown, Alexandra; Gajewski, Byron; Aaronson, Lauren; Mudaranthakam, Dinesh; Hunt, Suzanne; Berry, Scott; Quintana, Melanie; Pasnoor, Mamatha; Dimachkie, Mazen; Jawdat, Omar; Herbelin, Laura; Barohn, Richard Journal: Trials Issue: Volume 17:Issue 1(2016) Page Start: 1 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
2. ALSUntangled #65: glucocorticoid corticosteroids. Issue 3 (3rd April 2023) Authors: Goslinga, Jill Ann; Terrelonge, Mark; Bedlack, Richard; Barkhaus, Paul; Barnes, Benjamin; Bertorini, Tulio; Bromberg, Mark; Carter, Gregory; Chen, Amy; Crayle, Jesse; Dimachkie, Mazen; Jiang, Leanne; Levitsky, Gleb; Lund, Isaac; Martin, Sarah; Mcdermott, Christopher; Pattee, Gary; Pierce, Kaitlyn... Journal: Amyotrophic lateral sclerosis and frontotemporal degeneration Issue: Volume 24:Issue 3/4(2023) Page Start: 351 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
3. Amifampridine phosphate (Firdapse®) is effective and safe in a phase 3 clinical trial in LEMS. Issue 5 (3rd March 2016) Authors: Oh, Shin J; Shcherbakova, Natalya; Kostera‐Pruszczyk, Anna; Alsharabati, Mohammad; Dimachkie, Mazen; Blanco, Jose Munoz; Brannagan, Thomas; Lavrnić, Dragana; Shieh, Perry B; Vial, Christophe; Meisel, Andreas; Komoly, Samuel; Schoser, Benedikt; Sivakumar, Kumaraswamy; So, Yuen Journal: Muscle & nerve Issue: Volume 53:Issue 5(2016) Page Start: 717 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
4. An instrumented timed up and go in facioscapulohumeral muscular dystrophy. Issue 3 (6th October 2017) Authors: Huisinga, Jessie; Bruetsch, Adam; Mccalley, Ayla; Currence, Melissa; Herbelin, Laura; Jawdat, Omar; Pasnoor, Mamatha; Dimachkie, Mazen; Barohn, Richard; Statland, Jeffrey Journal: Muscle & nerve Issue: Volume 57:Issue 3(2018) Page Start: 503 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
5. Building efficient comparative effectiveness trials through adaptive designs, utility functions, and accrual rate optimization: finding the sweet spot. (7th January 2015) Authors: Gajewski, Byron J.; Berry, Scott M.; Quintana, Melanie; Pasnoor, Mamatha; Dimachkie, Mazen; Herbelin, Laura; Barohn, Richard Journal: Statistics in medicine Issue: Volume 34:Number 7(2015) Page Start: 1134 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
6. Long-term effect of thymectomy plus prednisone versus prednisone alone in patients with non-thymomatous myasthenia gravis: 2-year extension of the MGTX randomised trial. Issue 3 (March 2019) Authors: Wolfe, Gil I; Kaminski, Henry J; Aban, Inmaculada B; Minisman, Greg; Kuo, Hui-Chien; Marx, Alexander; Ströbel, Philipp; Mazia, Claudio; Oger, Joel; Cea, J Gabriel; Heckmann, Jeannine M; Evoli, Amelia; Nix, Wilfred; Ciafaloni, Emma; Antonini, Giovanni; Witoonpanich, Rawiphan; King, John O; Beydoun... Journal: Lancet neurology Issue: Volume 18:Issue 3(2019) Page Start: 259 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
7. Myopathies. (2014) Other Names: Dimachkie, Mazen Record Type: Book Extent: 1 online resource (305 pages) View Content: Available online (eLD content is only available in our Reading Rooms) ↗
8. North America and South America (NA-SA) neuropathy project. (1st August 2013) Authors: Pasnoor, Mamatha; Nascimento, Osvaldo J. M.; Trivedi, Jaya; Wolfe, Gil I.; Nations, Sharon; Herbelin, Laura; de Freitas, M. G.; Quintanilha, Giseli; Khan, Saud; Dimachkie, Mazen; Barohn, Richard Journal: International journal of neuroscience Issue: Volume 123:Number 8(2013:Aug.) Page Start: 563 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
9. Safety and efficacy of cipaglucosidase alfa plus miglustat versus alglucosidase alfa plus placebo in late-onset Pompe disease (PROPEL): an international, randomised, double-blind, parallel-group, phase 3 trial. Issue 12 (December 2021) Authors: Schoser, Benedikt; Roberts, Mark; Byrne, Barry J; Sitaraman, Sheela; Jiang, Hai; Laforêt, Pascal; Toscano, Antonio; Castelli, Jeff; Díaz-Manera, Jordi; Goldman, Mitchell; van der Ploeg, Ans T; Bratkovic, Drago; Kuchipudi, Srilakshmi; Mozaffar, Tahseen; Kishnani, Priya S; Sebok, Agnes; Pestronk, A... Journal: Lancet neurology Issue: Volume 20:Issue 12(2021) Page Start: 1027 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
10. Safety and efficacy of zilucoplan in patients with generalised myasthenia gravis (RAISE): a randomised, double-blind, placebo-controlled, phase 3 study. Issue 5 (May 2023) Authors: Howard, James F; Bresch, Saskia; Genge, Angela; Hewamadduma, Channa; Hinton, John; Hussain, Yessar; Juntas-Morales, Raul; Kaminski, Henry J; Maniaol, Angelina; Mantegazza, Renato; Masuda, Masayuki; Sivakumar, Kumaraswamy; Śmiłowski, Marek; Utsugisawa, Kimiaki; Vu, Tuan; Weiss, Michael D; Zajda, M... Journal: Lancet neurology Issue: Volume 22:Issue 5(2023) Page Start: 395 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗