1. A novel germline variant in PIK3R1 results in SHORT syndrome associated with TAL/LMO T‐cell acute lymphoblastic leukemia. Issue 12 (30th September 2020) Authors: Marzollo, Antonio; Maestrini, Giacomo; La Starza, Roberta; Elia, Loredana; Malfona, Francesco; Pierini, Tiziana; Tretti Parenzan, Caterina; Coppe, Alessandro; Bortoluzzi, Stefania; Biffi, Alessandra; Mecucci, Cristina; Bresolin, Silvia; Testi, Anna Maria Journal: American journal of hematology Issue: Volume 95:Issue 12(2020:Dec.) Page Start: E335 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
2. An innovative hematopoietic stem cell gene therapy approach benefits CLN1 disease in the mouse model. Issue 4 (6th March 2023) Authors: Peviani, Marco; Das, Sabyasachi; Patel, Janki; Jno‐Charles, Odella; Kumar, Rajesh; Zguro, Ana; Mathews, Tyler D; Cabras, Paolo; Milazzo, Rita; Cavalca, Eleonora; Poletti, Valentina; Biffi, Alessandra Journal: EMBO molecular medicine Issue: Volume 15:Issue 4(2023) Page Start: n/a Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
3. Biodegradable polymeric nanoparticles administered in the cerebrospinal fluid: Brain biodistribution, preferential internalization in microglia and implications for cell-selective drug release. (July 2019) Authors: Peviani, Marco; Capasso Palmiero, Umberto; Cecere, Francesca; Milazzo, Rita; Moscatelli, Davide; Biffi, Alessandra Journal: Biomaterials Issue: Volume 209(2019) Page Start: 25 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
4. Cellular magnetic resonance with iron oxide nanoparticles: long-term persistence of SPIO signal in the CNS after transplanted cell death. (2014) Authors: Cianciaruso, Chiara; Pagani, Antonella; Martelli, Cristina; Bacigaluppi, Marco; Leonardo Squadrito, Mario; Lo Dico, Alessia; De Palma, Michele; Furlan, Roberto; Lucignani, Giovanni; Falini, Andrea; Biffi, Alessandra; Ottobrini, Luisa; Salvatore Politi, Letterio Journal: Nanomedicine Issue: Volume 9:Number 10(2014) Page Start: 1457 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
5. Childhood cancer in Italy: background, goals, and achievements of the Italian Paediatric Hematology Oncology Association (AIEOP). Issue 5 (October 2021) Authors: Zecca, Marco; Ferrari, Andrea; Quarello, Paola; Rabusin, Marco; Balduzzi, Adriana; Buldini, Barbara; Rostagno, Elena; Prete, Arcangelo; Favre, Claudio; Massimino, Maura; Biondi, Andrea; Porta, Fulvio; Biffi, Alessandra; Locatelli, Franco; Pession, Andrea; Fagioli, Franca Journal: Tumori Issue: Volume 107:Issue 5(2021) Page Start: 370 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
6. Droplet Digital PCR Improves IG-/TR-based MRD Risk Definition in Childhood B-cell Precursor Acute Lymphoblastic Leukemia. Issue 3 (24th March 2021) Authors: Della Starza, Irene; Nunes, Vittorio; Lovisa, Federica; Silvestri, Daniela; Cavalli, Marzia; Garofalo, Andrea; Campeggio, Mimma; De Novi, Lucia Anna; Soscia, Roberta; Oggioni, Carlotta; Mussolin, Lara; Biondi, Andrea; Guarini, Anna; Valsecchi, Maria Grazia; Conter, Valentino; Biffi, Alessandra; B... Journal: HemaSphere Issue: Volume 5:Issue 3(2021) Page Start: e543 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
7. Evaluating high power laser therapy (HPLT) as treatment for chemotherapy‐induced oral mucositis in paediatric patients with oncohematological diseases. Issue 3 (10th March 2023) Authors: Ludovichetti, Francesco Saverio; Costa, Giorgia; Signoriello, Anna Giulia; Stellini, Edoardo; Zerman, Nicoletta; Biffi, Alessandra; Mazzoleni, Sergio Journal: International journal of paediatric dentistry Issue: Volume 33:Issue 3(2023) Page Start: 269 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
8. Gene therapy for lysosomal storage disorders: a good start. (24th November 2015) Authors: Biffi, Alessandra Journal: Human molecular genetics Issue: Volume 25:Number R1(2016) Page Start: R65 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
9. Hematopoietic stem cell transplantation for metachromatic leukodystrophy. (August 2015) Authors: Lorioli, Laura; Biffi, Alessandra Journal: Expert opinion on orphan drugs Issue: Volume 3:Number 8(2015:Aug.) Page Start: 911 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
10. Histiocytic sarcoma arising in a child affected by Burkitt lymphoma, with t(8;14)(q24;q32) positivity in both tumors. (2nd January 2021) Authors: d'Amore, Emanuele S.G; Mainardi, Chiara; Mussolin, Lara; Carraro, Elisa; Alaggio, Rita; Lazzari, Elena; Fusetti, Stefano; Ghirotto, Cristina; Marzollo, Antonio; Biddeci, Giada; Toffolutti, Tiziana; Massano, Davide; Scarzello, Giovanni; Zuliani, Monica; Putti, Maria Caterina; Biffi, Alessandra; Pi... Journal: Pediatric hematology and oncology Issue: Volume 38:Number 1(2021) Page Start: 1 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗