Sardh, E., Balwani, M., Rees, D. C., Stein, P., Stölzel, U., Peiro, P. A., Bissell, D. M., Bonkovsky, H. L., Keel, S., Parker, C., Phillips, J. D., Silver, S., Windyga, J., D'Avola, D., Ross, G., Stewart, P., Ritchie, B., Harper, P., Wang, J., Langendonk, J., Ivanova, A., Horie, Y., Anderson, K. E., Ventura, P., Cappellini, M. D., Vassiliou, D., Monroy, S., Petrides, P. E., Adachi, T., Kuter, D., Scalera, S., Penz, C., Liu, S., Ko, J. J., Simon, A., & Gouya, L. (n.d.). s1169 Twelve-Month Interim Analysis of Efficacy and Safety of Givosiran, an Investigational RNAi Therapeutic for Acute Hepatic Porphyria, in the ENVISION Open Label Extension. American journal of gastroenterology, 115, S584–S585. http://access.bl.uk/ark:/81055/vdc_100168588635.0x000037