1. Efficacy and safety of givosiran for acute hepatic porphyria: 24‐month interim analysis of the randomized phase 3 ENVISION study. (16th November 2021) Authors: Ventura, Paolo; Bonkovsky, Herbert L.; Gouya, Laurent; Aguilera‐Peiró, Paula; Montgomery Bissell, D.; Stein, Penelope E.; Balwani, Manisha; Anderson, D. Karl E.; Parker, Charles; Kuter, David J.; Monroy, Susana; Oh, Jeeyoung; Ritchie, Bruce; Ko, John J.; Hua, Zhaowei; Sweetser, Marianne T.; Sardh... Journal: Liver international Issue: Volume 42:Number 1(2022) Page Start: 161 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
2. EXPLORE B: A prospective, long‐term natural history study of patients with acute hepatic porphyria with chronic symptoms. Issue 6 (18th September 2022) Authors: Cassiman, David; Kauppinen, Raili; Monroy, Susana; Lee, Ming‐Jen; Bonkovsky, Herbert L.; Thapar, Manish; Guillén‐Navarro, Encarna; Minder, Anna‐Elisabeth; Hale, Cecilia; Sweetser, Marianne T.; Ivanova, Aneta Journal: Journal of inherited metabolic disease Issue: Volume 45:Issue 6(2022) Page Start: 1163 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
3. Hyperhomocysteinemia in acute hepatic porphyria (AHP) and implications for treatment with givosiran. (2nd September 2022) Authors: Ventura, Paolo; Sardh, Eliane; Longo, Nicola; Balwani, Manisha; Plutzky, Jorge; Gouya, Laurent; Phillips, John; Rhyee, Sean; Fanelli, Mary-Jean; Sweetser, Marianne T.; Petrides, Petro E. Journal: Expert review of gastroenterology & hepatology Issue: Volume 16:Number 9(2022) Page Start: 879 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
4. Inside Front Cover. (19th January 2022) Authors: Ventura, Paolo; Bonkovsky, Herbert L.; Gouya, Laurent; Aguilera‐Peiró, Paula; Montgomery Bissell, D.; Stein, Penelope E.; Balwani, Manisha; Anderson, D. Karl E.; Parker, Charles; Kuter, David J.; Monroy, Susana; Oh, Jeeyoung; Ritchie, Bruce; Ko, John J.; Hua, Zhaowei; Sweetser, Marianne T.; Sardh... Journal: Liver international Issue: Volume 42:Number 1(2022) Page Start: ii Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
5. Issue Cover. (29th December 2021) Authors: Ventura, Paolo; Bonkovsky, Herbert L.; Gouya, Laurent; Aguilera‐Peiró, Paula; Montgomery Bissell, D.; Stein, Penelope E.; Balwani, Manisha; Anderson, D. Karl E.; Parker, Charles; Kuter, David J.; Monroy, Susana; Oh, Jeeyoung; Ritchie, Bruce; Ko, John J.; Hua, Zhaowei; Sweetser, Marianne T.; Sardh... Journal: Liver international Issue: Volume 42:Number 1(2022) Page Start: i Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
6. Patisiran, an RNAi therapeutic for patients with hereditary transthyretin‐mediated amyloidosis: Sub‐analysis in Japanese patients from the APOLLO study. Issue 5 (21st July 2020) Authors: Yamashita, Taro; Ueda, Mitsuharu; Koike, Haruki; Sekijima, Yoshiki; Yoshinaga, Tsuneaki; Kodaira, Minori; Katsuno, Masahisa; Sobue, Gen; Zhang, Xiaoping; White, Matthew T.; Sweetser, Marianne T.; Wang, Jing Jing; Ando, Yukio Journal: Neurology and clinical neuroscience Issue: Volume 8:Issue 5(2020:Sep.) Page Start: 251 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
7. Quality of life outcomes in APOLLO, the phase 3 trial of the RNAi therapeutic patisiran in patients with hereditary transthyretin-mediated amyloidosis. (2nd July 2020) Authors: Obici, Laura; Berk, John L.; González-Duarte, Alejandra; Coelho, Teresa; Gillmore, Julian; Schmidt, Hartmut H.-J.; Schilling, Matthias; Yamashita, Taro; Labeyrie, Céline; Brannagan, Thomas H.; Ajroud-Driss, Senda; Gorevic, Peter; Kristen, Arnt V.; Franklin, Jaclyn; Chen, Jihong; Sweetser, Mariann... Journal: Amyloid Issue: Volume 27:Number 3(2020) Page Start: 153 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
8. S1063 Disease Burden in Patients With Acute Hepatic Porphyria: Experience From the Phase 3 ENVISION Study. (October 2021) Authors: Wang, Bruce; Ventura, Paolo; Takase, Kei-ichiro; Thapar, Manish; Cassiman, David M.; Kubisch, Ilja; Hua, Zhaowei; Sweetser, Marianne T.; Balwani, Manisha Journal: American journal of gastroenterology Issue: Volume 116:Supplement(2021)ACG Annual Meeting Abstracts 1 Page Start: S504 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
9. S1170 Efficacy and Safety of Givosiran in Patients With Acute Hepatic Porphyria: 24-Month Interim Analysis of the Phase 3 ENVISION Randomized Clinical Trial. (October 2021) Authors: Bonkovsky, Herbert L.; Ventura, Paolo; Gouya, Laurent; Peiró, Paula Aguilera; Bissell, D. Montgomery; Stein, Penelope E.; Anderson, Karl E.; Monroy, Susana; Kuter, David J.; Oh, Jeeyoung; Ko, John J.; Hua, Zhaowei; Sweetser, Marianne T.; Sardh, Eliane Journal: American journal of gastroenterology Issue: Volume 116:Supplement(2021)ACG Annual Meeting Abstracts 1 Page Start: S545 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
10. S1171 EXPLORE Part B: A Prospective, International, Long-Term Natural History Study of Patients With Acute Hepatic Porphyria With Recurrent Symptoms. (October 2021) Authors: Cassiman, David M.; Kauppinen, Raili M.; Monroy, Susana; Lee, Ming-Jen; Bonkovsky, Herbert L.; FACG, ; Thapar, Manish; Guillén-Navarro, Encarna; Hua, Zhaowei; Sweetser, Marianne T.; Ivanova, Aneta V. Journal: American journal of gastroenterology Issue: Volume 116:Supplement(2021)ACG Annual Meeting Abstracts 1 Page Start: S546 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗