1. B.01 AVXS-101 gene-replacement therapy (GRT) for spinal muscular atrophy type 1 (SMA1): pivotal phase 3 study (STR1VE) update. (5th June 2019) Authors: Day, JW; Chiriboga, CA; Crawford, TO; Darras, BT; Finkel, RS; Connolly, AM; Iannaccone, ST; Kuntz, NL; Pena, LD; Schultz, M; Shieh, PB; Smith, EC; Feltner, DE; Ogrinc, FG; Macek, TA; Kernbauer, E; Muehring, LM; L'Italien, J; Sproule, DM; Kaspar, BK Journal: Canadian journal of neurological sciences Issue: Volume 46(2019)Supplement 1 Page Start: S10 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
2. B.01 AVXS-101 gene-replacement therapy (GRT) for spinal muscular atrophy type 1 (SMA1): pivotal phase 3 study (STR1VE) update. (June 2019) Authors: Day, JW; Chiriboga, CA; Crawford, TO; Darras, BT; Finkel, RS; Connolly, AM; Iannaccone, ST; Kuntz, NL; Pena, LD; Schultz, M; Shieh, PB; Smith, EC; Feltner, DE; Ogrinc, FG; Macek, TA; Kernbauer, E; Muehring, LM; L'Italien, J; Sproule, DM; Kaspar, BK Journal: Canadian journal of neurological sciences Issue: Volume 46(2019)Supplement 1 Page Start: S10 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
3. P.060 Time to treatment effect in Spinal Muscular Atrophy Type 1 (SMA1): an indirect comparison of treatments. (5th June 2019) Authors: Finkel, RS; Dabbous, O; Arjunji, R; Droege, M; Feltner, DE; Novack, A; Menier, M; Sproule, DM Journal: Canadian journal of neurological sciences Issue: Volume 46(2019)Supplement 1 Page Start: S30 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
4. P.060 Time to treatment effect in Spinal Muscular Atrophy Type 1 (SMA1): an indirect comparison of treatments. (June 2019) Authors: Finkel, RS; Dabbous, O; Arjunji, R; Droege, M; Feltner, DE; Novack, A; Menier, M; Sproule, DM Journal: Canadian journal of neurological sciences Issue: Volume 46(2019)Supplement 1 Page Start: S30 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
5. P.061 The value of AVXS-101 gene-replacement therapy for Spinal Muscular Atrophy Type 1 (SMA1). (5th June 2019) Authors: Dabbous, O; Sproule, DM; Feltner, DE; Droege, M; Khan, F; Arjunji, R Journal: Canadian journal of neurological sciences Issue: Volume 46(2019)Supplement 1 Page Start: S30 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
6. P.061 The value of AVXS-101 gene-replacement therapy for Spinal Muscular Atrophy Type 1 (SMA1). (June 2019) Authors: Dabbous, O; Sproule, DM; Feltner, DE; Droege, M; Khan, F; Arjunji, R Journal: Canadian journal of neurological sciences Issue: Volume 46(2019)Supplement 1 Page Start: S30 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
7. P.062 Burden of illness of spinal muscular atrophy (SMA): an update. (5th June 2019) Authors: Droege, M; Dabbous, O; Arjunji, R; Gauthier-Loiselle, M; Cloutier, M; Sproule, DM Journal: Canadian journal of neurological sciences Issue: Volume 46(2019)Supplement 1 Page Start: S30 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
8. P.062 Burden of illness of spinal muscular atrophy (SMA): an update. (June 2019) Authors: Droege, M; Dabbous, O; Arjunji, R; Gauthier-Loiselle, M; Cloutier, M; Sproule, DM Journal: Canadian journal of neurological sciences Issue: Volume 46(2019)Supplement 1 Page Start: S30 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
9. P.065 AVXS-101 gene-replacement therapy (GRT)) in presymptomatic spinal muscular atrophy (SMA): study update. (5th June 2019) Authors: Schultz, M; Swoboda, K; Farrar, M; McMillan, H; Parsons, J; Farrow, M; Ogrinc, FG; Feltner, DE; McGill, BE; Spector, SA; L'Italien, J; Sproule, DM; Strauss, KA Journal: Canadian journal of neurological sciences Issue: Volume 46(2019)Supplement 1 Page Start: S31 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
10. P.065 AVXS-101 gene-replacement therapy (GRT)) in presymptomatic spinal muscular atrophy (SMA): study update. (June 2019) Authors: Schultz, M; Swoboda, K; Farrar, M; McMillan, H; Parsons, J; Farrow, M; Ogrinc, FG; Feltner, DE; McGill, BE; Spector, SA; L'Italien, J; Sproule, DM; Strauss, KA Journal: Canadian journal of neurological sciences Issue: Volume 46(2019)Supplement 1 Page Start: S31 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗