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2. Biochemical and clinical response after umbilical cord blood transplant in a boy with early childhood‐onset beta‐mannosidosis. Issue 7 (21st May 2019)

4. Current directions in tau research: Highlights from Tau 2020. Issue 5 (28th September 2021)

5. De Novo DNM1L Variant in a Teenager With Progressive Paroxysmal Dystonia and Lethal Super-refractory Myoclonic Status Epilepticus. (September 2018)

6. Efficacy and safety of arimoclomol in Niemann‐Pick disease type C: Results from a double‐blind, randomised, placebo‐controlled, multinational phase 2/3 trial of a novel treatment. Issue 6 (7th September 2021)

8. Expanded genetic insight and clinical experience of DNMT1-complex disorder. (August 2020)

9. Free sialic acid storage disorder: Progress and promise. (11th June 2021)

10. Functional characterization of a GFAP variant of uncertain significance in an Alexander disease case within the setting of an individualized medicine clinic. Issue 9 (15th August 2016)