1. Update on safety and efficacy of lentiviral hematopoietic stem cell gene therapy (HSC-GT) for metachromatic leukodystrophy (MLD). (June 2017) Authors: Fumagalli, F.; Calbi, V.; Zambon, A.; Ciotti, F.; Lorioli, L.; Sessa, M.; Sarzana, M.; Canale, S.; Antonioli, G.; Medaglini, S.; Del Carro, U.; Quattrini, A.; Baldoli, C.; Martino, S.; Di Serio, C.; Ciceri, F.; Naldini, L.; Natali Sora, M.G.; Biffi, A.; Aiuti, A. Journal: European journal of paediatric neurology Issue: Volume 21(2017)Supplement 1 Page Start: e20 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗