Update on safety and efficacy of lentiviral hematopoietic stem cell gene therapy (HSC-GT) for metachromatic leukodystrophy (MLD). (June 2017)

• Record Type: Journal Article
• Authors: Fumagalli, F.; Calbi, V.; Zambon, A.; Ciotti, F.; Lorioli, L.; Sessa, M.; Sarzana, M.; Canale, S.; Antonioli, G.; Medaglini, S.; Del Carro, U.; Quattrini, A.; Baldoli, C.; Martino, S.; Di Serio, C.; Ciceri, F.; Naldini, L.; Natali Sora, M.G.; Biffi, A.; Aiuti, A.
• Is Part Of: European journal of paediatric neurology. Volume 21(2017)Supplement 1
• Page Start: e20
• Publication Date: 2017-06
• Subjects: Pediatric neurology -- Periodicals; Nervous System Diseases -- Periodicals; Child -- Periodicals; Infant -- Periodicals; Neurologie pédiatrique -- Périodiques; Pediatric neurology; Electronic journals; Periodicals; Electronic journals; 618.928
• DOI: 10.1016/j.ejpn.2017.04.986
• Languages: English
• ISSNs: 1090-3798