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You searched for: Author/Creator Goffrini, Paola

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1. A novel de novo dominant mutation in ISCU associated with mitochondrial myopathy. Issue 12 (27th October 2017)

3. Bi‐allelic KARS1 pathogenic variants affecting functions of cytosolic and mitochondrial isoforms are associated with a progressive and multisystem disease. Issue 6 (11th May 2021)

4. Clinical, radiological, and genetic characteristics of 16 patients with ACO2 gene defects: Delineation of an emerging neurometabolic syndrome. Issue 2 (28th January 2019)

5. Clinical‐genetic features and peculiar muscle histopathology in infantile DNM1L‐related mitochondrial epileptic encephalopathy. Issue 5 (9th March 2019)

6. Defective PITRM1 mitochondrial peptidase is associated with Aβ amyloidotic neurodegeneration. Issue 3 (23rd December 2015)

7. Drug repositioning as a therapeutic strategy for neurodegenerations associated with OPA1 mutations. (24th November 2020)

9. LBSL: Case Series and DARS2 Variant Analysis in Early Severe Forms With Unexpected Presentations. (April 2021)

10. Molecular genetic investigations identify new clinical phenotypes associated with BCS1L-related mitochondrial disease. (22nd August 2019)