1. Effects of miglustat therapy on neurological disorder and survival in early-infantile Niemann-Pick disease type C: A national French retrospective study. (June 2017) Authors: Freihuber, C.; Dahmani, B.; Brassier, A.; Broue, P.; Cances, C.; Chabrol, B.; Eyer, D.; Labarthe, F.; Latour, P.; Levade, T.; Pichard, S.; Sevin, C.; Vanier, M.T.; Héron, B. Journal: European journal of paediatric neurology Issue: Volume 21(2017)Supplement 1 Page Start: e2 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗