Effects of miglustat therapy on neurological disorder and survival in early-infantile Niemann-Pick disease type C: A national French retrospective study. (June 2017)

• Record Type: Journal Article
• Authors: Freihuber, C.; Dahmani, B.; Brassier, A.; Broue, P.; Cances, C.; Chabrol, B.; Eyer, D.; Labarthe, F.; Latour, P.; Levade, T.; Pichard, S.; Sevin, C.; Vanier, M.T.; Héron, B.
• Is Part Of: European journal of paediatric neurology. Volume 21(2017)Supplement 1
• Page Start: e2
• Publication Date: 2017-06
• Subjects: Pediatric neurology -- Periodicals; Nervous System Diseases -- Periodicals; Child -- Periodicals; Infant -- Periodicals; Neurologie pédiatrique -- Périodiques; Pediatric neurology; Electronic journals; Periodicals; Electronic journals; 618.928
• DOI: 10.1016/j.ejpn.2017.04.872
• Languages: English
• ISSNs: 1090-3798