1. Cas9/sgRNA selective targeting of the P23H Rhodopsin mutant allele for treating retinitis pigmentosa by intravitreal AAV9.PHP.B-based delivery. (21st December 2017) Authors: Giannelli, Serena G; Luoni, Mirko; Castoldi, Valerio; Massimino, Luca; Cabassi, Tommaso; Angeloni, Debora; Demontis, Gian Carlo; Leocani, Letizia; Andreazzoli, Massimiliano; Broccoli, Vania Journal: Human molecular genetics Issue: Volume 27:Number 5(2018:Mar. 01) Page Start: 761 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
2. Coenzyme A corrects pathological defects in human neurons of PANK2‐associated neurodegeneration. Issue 10 (11th August 2016) Authors: Orellana, Daniel I; Santambrogio, Paolo; Rubio, Alicia; Yekhlef, Latefa; Cancellieri, Cinzia; Dusi, Sabrina; Giannelli, Serena G; Venco, Paola; Mazzara, Pietro G; Cozzi, Anna; Ferrari, Maurizio; Garavaglia, Barbara; Taverna, Stefano; Tiranti, Valeria; Broccoli, Vania; Levi, Sonia Journal: EMBO molecular medicine Issue: Volume 8:Issue 10(2016) Page Start: 1197 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
3. GABAergic Neuronal Precursor Grafting: Implications in Brain Regeneration and Plasticity. (20th June 2011) Authors: Alvarez Dolado, Manuel; Broccoli, Vania Other Names: Di Cristo Graziella Academic Editor. Journal: Neural plasticity Issue: Volume 2011(2011) Page Start: Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
4. Generation of Human Induced Pluripotent Stem Cell-Derived Bona Fide Neural Stem Cells for Ex Vivo Gene Therapy of Metachromatic Leukodystrophy. (16th September 2016) Authors: Meneghini, Vasco; Frati, Giacomo; Sala, Davide; De Cicco, Silvia; Luciani, Marco; Cavazzin, Chiara; Paulis, Marianna; Mentzen, Wieslawa; Morena, Francesco; Giannelli, Serena; Sanvito, Francesca; Villa, Anna; Bulfone, Alessandro; Broccoli, Vania; Martino, Sabata; Gritti, Angela Journal: Stem cells translational medicine Issue: Volume 6:Number 2(2017) Page Start: 352 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
5. Generation of Human Induced Pluripotent Stem Cell‐Derived Bona Fide Neural Stem Cells for Ex Vivo Gene Therapy of Metachromatic Leukodystrophy. (16th September 2016) Authors: Meneghini, Vasco; Frati, Giacomo; Sala, Davide; De Cicco, Silvia; Luciani, Marco; Cavazzin, Chiara; Paulis, Marianna; Mentzen, Wieslawa; Morena, Francesco; Giannelli, Serena; Sanvito, Francesca; Villa, Anna; Bulfone, Alessandro; Broccoli, Vania; Martino, Sabata; Gritti, Angela Journal: Stem cells translational medicine Issue: Volume 6:Number 2(2017) Page Start: 352 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
6. Histone modifications controlling native and induced neural stem cell identity. (October 2015) Authors: Broccoli, Vania; Colasante, Gaia; Sessa, Alessandro; Rubio, Alicia Journal: Current opinion in genetics & development Issue: Volume 34(2015) Page Start: 95 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
7. I10 A genome-wide screening in pluripotent cells identifies MTF1 as a novel suppressor of mutant huntingtin toxicity. (12th September 2022) Authors: Ferlazzo, Giorgia Maria; Gambetta, Anna Maria; Amato, Sonia; Cannizzaro, Noemi; Angiolillo, Silvia; Arboit, Mattia; Galimberti, Elena; Pflug, Florian; Carbognin, Elena; Luoni, Mirko; Giannelli, Serena; Pepe, Giuseppe; Capocci, Luca; Pardo, Alba Di; Broccoli, Vania; Leeb, Martin; Moro, Enrico; Mag... Journal: Journal of neurology, neurosurgery and psychiatry Issue: Volume 93(2022)Supplement 1 Page Start: A88 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
8. MSEL‐1L deficiency affects vasculogenesis and neural stem cell lineage commitment. Issue 4 (12th September 2017) Authors: Cardano, Marina; Diaferia, Giuseppe R.; Conti, Luciano; Baronchelli, Simona; Sessa, Alessandro; Broccoli, Vania; Barbieri, Andrea; De Blasio, Pasquale; Biunno, Ida Journal: Journal of cellular physiology Issue: Volume 233:Issue 4(2018:Apr.) Page Start: 3152 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
9. Overcoming the hurdles for a reproducible generation of human functionally mature reprogrammed neurons. (June 2015) Authors: Broccoli, Vania; Rubio, Alicia; Taverna, Stefano; Yekhlef, Latefa Journal: Experimental biology and medicine Issue: Volume 240:Number 6(2015:Jun.) Page Start: 787 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
10. Rapid Generation of Functional Dopaminergic Neurons From Human Induced Pluripotent Stem Cells Through a Single‐Step Procedure Using Cell Lineage Transcription Factors. (8th May 2013) Authors: Theka, Ilda; Caiazzo, Massimiliano; Dvoretskova, Elena; Leo, Damiana; Ungaro, Federica; Curreli, Sebastiano; Managò, Francesca; Dell'Anno, Maria Teresa; Pezzoli, Gianni; Gainetdinov, Raul R.; Dityatev, Alexander; Broccoli, Vania Journal: Stem cells translational medicine Issue: Volume 2:Number 6(2013) Page Start: 473 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗