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Terlizzi, V. et al. (2021). Ex vivo model predicted in vivo efficacy of CFTR modulator therapy in a child with rare genotype. Molecular genetics & genomic medicine. 9 (4), p. n/a. [Online].
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Terlizzi, V. et al. (2021). Ex vivo model predicted in vivo efficacy of CFTR modulator therapy in a child with rare genotype. Molecular genetics & genomic medicine. 9 (4), p. n/a. [Online].