Intra cerebral administration of AAVrh-10 carrying human SGSH and SUMF1 cDNAs in children with MPSIIIA disease: Long term follow-up of a phase I–II trial. (June 2017) - Deiva, Kumaran; Maurey, Helene; Sevin, Caroline; Cormary, Carine; Leroy, Carole; Bekkali, Soraya; Zerah, Michel; Tardieu, Marc