Translational research in muscular dystrophy. (2016)

• Record Type: Book
• Further Information: Note: Shin'ichi Takeda, Yuko Miyagoe-Suzuki, Madoka Mori-Yoshimura, editors.
• Editors: Takeda, Shinʾichi; Miyagoe-Suzuki, Yuko; Mori-Yoshimura, Madoka
• Contents: 1. Fukuyama congenital muscular dystrophy -- Clinical aspects -- 2. ?-Dystroglycanopathy -- 3. Myotonic dystrophy -- 4. Molecular pathogenesis and therapeutic strategy in GNE myopathy -- 5. Targeting the type I TGF-? receptor for treating caveolin-3-deficient autosomal dominant limb-girdle muscular dystrophy type 1C and muscle wasting disorders -- 6. Translational Research in Nucleic Acid Therapies for Muscular Dystrophies -- 7. Toward regenerative medicine for muscular dystrophies-Lessons from regeneration processes- -- 8. Stem cell-based therapy for Duchenne muscular dystrophy -- 9. Therapeutic approach of iPS cell technology for treating muscular dystrophy -- 10. Clinical aspects of GNE myopathy and translational medicine -- 11. Patient registries for international harmonized clinical development -- 12. Muscular Dystrophy Clinical Trial Network in Japan -- 13. Translational research on DMD in Japan From mice to exploratory investigator{u2013}initiated clinical trial in humans. .
• Publisher Details: Tokyo : Springer
• Publication Date: 2016
• Extent: 1 online resource (viii, 199 pages), illustrations (some color)
• Subjects: 616.7/48; Muscular dystrophy -- Research; Muscular dystrophy -- Research; HEALTH & FITNESS / Diseases / General; MEDICAL / Clinical Medicine; MEDICAL / Diseases; MEDICAL / Evidence-Based Medicine; MEDICAL / Internal Medicine; Medicine & Public Health; Neurology; Molecular Medicine; Gene Therapy; Muscular Dystrophy, Duchenne; Electronic books; Electronic books
• Languages: English
• ISBNs: 9784431556787; 4431556788
• Related ISBNs: 9784431556770; 443155677X
• Notes: Note: Online resource; title from PDF title page (SpringerLink, viewed February 8, 2016).
• Access Rights: Legal Deposit; Only available on premises controlled by the deposit library and to one user at any one time; The Legal Deposit Libraries (Non-Print Works) Regulations (UK).
• Access Usage: Restricted: Printing from this resource is governed by The Legal Deposit Libraries (Non-Print Works) Regulations (UK) and UK copyright law currently in force.