1. A pediatric quantitative systems pharmacology model of neurofilament trafficking in spinal muscular atrophy treated with the antisense oligonucleotide nusinersen. (5th December 2022) Authors: Paris, Alessio; Bora, Pranami; Parolo, Silvia; MacCannell, Drew; Monine, Michael; van der Munnik, Nick; Tong, Xiao; Eraly, Satish; Berger, Zdenek; Graham, Danielle; Ferguson, Toby; Domenici, Enrico; Nestorov, Ivan; Marchetti, Luca Journal: CPT: pharmacometrics & systems pharmacology Issue: Volume 12:Number 2(2023) Page Start: 196 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗