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1. Mitapivat in adult patients with pyruvate kinase deficiency receiving regular transfusions (ACTIVATE-T): a multicentre, open-label, single-arm, phase 3 trial. Issue 10 (October 2022)

2. The Pyruvate Kinase Deficiency Global Longitudinal (Peak) Registry: rationale and study design. Issue 3 (23rd March 2023)