1. Nusinersen in adults with 5q spinal muscular atrophy: a non-interventional, multicentre, observational cohort study. Issue 4 (April 2020) Authors: Hagenacker, Tim; Wurster, Claudia D; Günther, René; Schreiber-Katz, Olivia; Osmanovic, Alma; Petri, Susanne; Weiler, Markus; Ziegler, Andreas; Kuttler, Josua; Koch, Jan C; Schneider, Ilka; Wunderlich, Gilbert; Schloss, Natalie; Lehmann, Helmar C; Cordts, Isabell; Deschauer, Marcus; Lingor, Paul; ... Journal: Lancet neurology Issue: Volume 19:Issue 4(2020) Page Start: 317 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗