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Author/Creator Whitley, Chester

1. Long-term outcomes of systemic therapies for Hurler syndrome: an international multicenter comparison. (November 2018)

Authors:
Eisengart, Julie; Rudser, Kyle; Xue, Yong; Orchard, Paul; Miller, Weston; Lund, Troy; Van der Ploeg, Ans; Mercer, Jean; Jones, Simon; Mengel, Karl Eugen; Gökce, Seyfullah; Guffon, Nathalie; Giugliani, Roberto; de Souza, Carolina; Shapiro, Elsa; Whitley, Chester
Journal:
Genetics in medicine
Issue:
Volume 20:Number 11(2018)
Page Start:
1423
Record Type:
Journal Article
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Available online (eLD content is only available in our Reading Rooms) ↗

2. Safety and efficacy of avalglucosidase alfa versus alglucosidase alfa in patients with late-onset Pompe disease (COMET): a phase 3, randomised, multicentre trial. Issue 12 (December 2021)

Authors:
Diaz-Manera, Jordi; Kishnani, Priya S; Kushlaf, Hani; Ladha, Shafeeq; Mozaffar, Tahseen; Straub, Volker; Toscano, Antonio; van der Ploeg, Ans T; Berger, Kenneth I; Clemens, Paula R; Chien, Yin-Hsiu; Day, John W; Illarioshkin, Sergey; Roberts, Mark; Attarian, Shahram; Borges, Joao Lindolfo; Bouhou...
Journal:
Lancet neurology
Issue:
Volume 20:Issue 12(2021)
Page Start:
1012
Record Type:
Journal Article
View Content:
Available online (eLD content is only available in our Reading Rooms) ↗

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