1. MCOLN1 gene therapy corrects neurologic dysfunction in the mouse model of mucolipidosis IV. Issue 10 (5th April 2021) Authors: DeRosa, Samantha; Salani, Monica; Smith, Sierra; Sangster, Madison; Miller-Browne, Victoria; Wassmer, Sarah; Xiao, Ru; Vandenberghe, Luk; Slaugenhaupt, Susan; Misko, Albert; Grishchuk, Yulia Journal: Human molecular genetics Issue: Volume 30:Issue 10(2021) Page Start: 908 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗