1. Adults with spinal muscular atrophy: a large-scale natural history study shows gender effect on disease. Issue 12 (11th October 2022) Authors: Maggi, Lorenzo; Bello, Luca; Bonanno, Silvia; Govoni, Alessandra; Caponnetto, Claudia; Passamano, Luigia; Grandis, Marina; Trojsi, Francesca; Cerri, Federica; Gardani, Alice; Ferraro, Manfredi; Gadaleta, Giulio; Zangaro, Vittoria; Caumo, Luca; Maioli, Mariantonietta; Tanel, Raffaella; Saccani, El... Journal: Journal of neurology, neurosurgery and psychiatry Issue: Volume 93:Issue 12(2022) Page Start: 1253 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
2. Nusinersen safety and effects on motor function in adult spinal muscular atrophy type 2 and 3. Issue 11 (11th September 2020) Authors: Maggi, Lorenzo; Bello, Luca; Bonanno, Silvia; Govoni, Alessandra; Caponnetto, Claudia; Passamano, Luigia; Grandis, Marina; Trojsi, Francesca; Cerri, Federica; Ferraro, Manfredi; Bozzoni, Virginia; Caumo, Luca; Piras, Rachele; Tanel, Raffaella; Saccani, Elena; Meneri, Megi; Vacchiano, Veria; Ricci... Journal: Journal of neurology, neurosurgery and psychiatry Issue: Volume 91:Issue 11(2020) Page Start: 1166 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
3. Prevalence of Spinal Muscular Atrophy in the Era of Disease-Modifying Therapies: An Italian Nationwide Survey. (14th March 2023) Authors: Coratti, Giorgia; Ricci, Martina; Capasso, Anna; D'amico, Adele; Sansone, Valeria; Bruno, Claudio; Messina, Sonia; Ricci, Federica; Mongini, Tiziana; Coccia, Michela; Siciliano, Gabriele; Pegoraro, Elena; Turri, Mara; Filosto, Massimiliano; Comi, Giacomo; Masson, Riccardo; Maggi, Lorenzo; Bruno, ... Journal: Neurology Issue: Volume 100:Number 11(2023) Page Start: 522 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗