1. Mechanistic convergence and shared therapeutic targets in Niemann‐Pick disease. Issue 3 (5th December 2019) Authors: Colaco, Alexandria; Kaya, Ecem; Adriaenssens, Elias; Davis, Lianne C.; Zampieri, Stefania; Fernández‐Suárez, María E.; Tan, Chong Y.; Deegan, Patrick B.; Porter, Forbes D.; Galione, Antony; Bembi, Bruno; Dardis, Andrea; Platt, Frances M. Journal: Journal of inherited metabolic disease Issue: Volume 43:Issue 3(2020) Page Start: 574 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗