1. MO034A SUBGROUP ANALYSIS OF FEMALE PATIENTS IN A PHASE 3 OPEN-LABEL STUDY TO ASSESS THE SAFETY AND EFFICACY OF PEGUNIGALSIDASE ALFA IN PATIENTS WITH FABRY DISEASE PREVIOUSLY TREATED WITH AGALSIDASE ALFA. (29th May 2021) Authors: Hughes, Derralynn; Dostalova, Gabriela; Nicholls, Kathy; West, Michael; Tã¸ndel, Camilla; Jovanovic, Ana; Castellano, Pilar Giraldo; Vujkovac, Bojan; Geberhiwot, Tarekegn; Almon, Einat; Alon, Sari; Szlaifer, Mali; Chertkoff, Raul; Linhart, Ales Journal: Nephrology dialysis transplantation Issue: Volume 36(2021)Supplement 1 Page Start: Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
2. Novel Orally Administered Recombinant Anti-TNF Alpha Fusion Protein for the Treatment of Ulcerative Colitis: Results From a Phase 2a Clinical Trial. Issue 2 (February 2021) Authors: Almon, Einat; Shaaltiel, Yoseph; Sbeit, Wisam; Fich, Alex; Schwartz, Doron; Waterman, Mattitiahu; Szlaifer, Mali; Reuveni, Hadar; Amit-Cohen, Bat-chen; Alon, Sari; Chertkoff, Raul; Paz, Alona; Ilan, Yaron Journal: Journal of clinical gastroenterology Issue: Volume 55:Issue 2(2021) Page Start: Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
3. Pegunigalsidase alfa, a novel PEGylated enzyme replacement therapy for Fabry disease, provides sustained plasma concentrations and favorable pharmacodynamics: A 1‐year Phase 1/2 clinical trial. Issue 3 (8th April 2019) Authors: Schiffmann, Raphael; Goker‐Alpan, Ozlem; Holida, Myrl; Giraldo, Pilar; Barisoni, Laura; Colvin, Robert B.; Jennette, Charles J.; Maegawa, Gustavo; Boyadjiev, Simeon A.; Gonzalez, Derlis; Nicholls, Kathy; Tuffaha, Ahmad; Atta, Mohamed G.; Rup, Bonita; Charney, Martha R.; Paz, Alona; Szlaifer, Mali... Journal: Journal of inherited metabolic disease Issue: Volume 42:Issue 3(2019) Page Start: 534 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗