1. Effects of Patisiran, an RNA Interference Therapeutic, on Cardiac Parameters in Patients With Hereditary Transthyretin-Mediated Amyloidosis: Analysis of the APOLLO Study. Issue 4 (22nd January 2019) Authors: Solomon, Scott D.; Adams, David; Kristen, Arnt; Grogan, Martha; González-Duarte, Alejandra; Maurer, Mathew S.; Merlini, Giampaolo; Damy, Thibaud; Slama, Michel S.; Brannagan, Thomas H.; Dispenzieri, Angela; Berk, John L.; Shah, Amil M.; Garg, Pushkal; Vaishnaw, Akshay; Karsten, Verena; Chen, Jiho... Journal: Circulation Issue: Volume 139:Issue 4(2019) Page Start: Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
2. Liver Transplantation for Hereditary Transthyretin Amyloidosis. Issue 9 (September 2015) Authors: Ericzon, Bo-Göran; Wilczek, Henryk E.; Larsson, Marie; Wijayatunga, Priyantha; Stangou, Arie; Pena, João Rodrigues; Furtado, Emanuel; Barroso, Eduardo; Daniel, Jorge; Samuel, Didier; Adam, Rene; Karam, Vincent; Poterucha, John; Lewis, David; Ferraz-Neto, Ben-Hur; Cruz, Márcia Waddington; Munar-Qu... Journal: Transplantation Issue: Volume 99:Issue 9(2015) Page Start: Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
3. Liver Transplantation for Hereditary Transthyretin Amyloidosis: After 20 Years Still the Best Therapeutic Alternative?. Issue 9 (September 2015) Authors: Ericzon, Bo-Göran; Wilczek, Henryk E.; Larsson, Marie; Wijayatunga, Priyantha; Stangou, Arie; Pena, João Rodrigues; Furtado, Emanuel; Barroso, Eduardo; Daniel, Jorge; Samuel, Didier; Adam, Rene; Karam, Vincent; Poterucha, John; Lewis, David; Ferraz-Neto, Ben-Hur; Cruz, Márcia Waddington; Munar-Qu... Journal: Transplantation Issue: Volume 99:Issue 9(2015) Page Start: Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
4. Long-term safety and efficacy of patisiran for hereditary transthyretin-mediated amyloidosis with polyneuropathy: 12-month results of an open-label extension study. Issue 1 (January 2021) Authors: Adams, David; Polydefkis, Michael; González-Duarte, Alejandra; Wixner, Jonas; Kristen, Arnt V; Schmidt, Hartmut H; Berk, John L; Losada López, Inés Asunción; Dispenzieri, Angela; Quan, Dianna; Conceição, Isabel M; Slama, Michel S; Gillmore, Julian D; Kyriakides, Theodoros; Ajroud-Driss, Senda; Wa... Journal: Lancet neurology Issue: Volume 20:Issue 1(2021) Page Start: 49 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
5. Long-term safety and efficacy of patisiran for hereditary transthyretin-mediated amyloidosis with polyneuropathy: 12-month results of an open-label extension study. Issue 1 (January 2021) Authors: Adams, David; Polydefkis, Michael; González-Duarte, Alejandra; Wixner, Jonas; Kristen, Arnt V; Schmidt, Hartmut H; Berk, John L; Losada López, Inés Asunción; Dispenzieri, Angela; Quan, Dianna; Conceição, Isabel M; Slama, Michel S; Gillmore, Julian D; Kyriakides, Theodoros; Ajroud-Driss, Senda; Wa... Journal: Lancet neurology Issue: Volume 20:Issue 1(2021) Page Start: 49 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
6. PATISIRAN PH 2 OPEN-LABEL EXTENSION STUDY IN FAMILIAL AMYLOIDOTIC POLYNEUROPATHY. Issue 12 (15th November 2016) Authors: Schmidt, Hartmut; Adams, David; Coelho, Teresa; Conceicao, Isabel; Waddington-Cruz, Marcia; Buades, Juan; Campistol, Josep; Pouget, Jean; Gollob, Jared; Suhr, Ole Journal: Journal of neurology, neurosurgery and psychiatry Issue: Volume 87:Issue 12(2016) Page Start: e1 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
7. Phase 2 open-label extention (OLE) study of patisiran, an investigational siRNA agent for familial amyloidotic polyneuropathy (FAP). Issue 1 (December 2015) Authors: Adams, David; Suhr, Ole; Conceicao, Isabel; Waddington-Cruz, Marcia; Schmidt, Hartmut; Buades, Juan; Campistol, Josep; Coehlo, Teresa Journal: Orphanet journal of rare diseases Issue: Volume 9:Issue 1(2014) Page Start: 1 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
8. Preliminary assessment of neuropathy progression in patients with hereditary ATTR amyloidosis after orthotopic liver transplantation (OLT). Issue 1 (December 2015) Authors: Adams, David; Buades, Juan; Suhr, Ole; Obici, Laura; Coelho, Teresa Journal: Orphanet journal of rare diseases Issue: Volume 9:Issue 1(2014) Page Start: 1 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗