1. P.065 AVXS-101 gene-replacement therapy (GRT)) in presymptomatic spinal muscular atrophy (SMA): study update. (5th June 2019) Authors: Schultz, M; Swoboda, K; Farrar, M; McMillan, H; Parsons, J; Farrow, M; Ogrinc, FG; Feltner, DE; McGill, BE; Spector, SA; L'Italien, J; Sproule, DM; Strauss, KA Journal: Canadian journal of neurological sciences Issue: Volume 46(2019)Supplement 1 Page Start: S31 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
2. P.065 AVXS-101 gene-replacement therapy (GRT)) in presymptomatic spinal muscular atrophy (SMA): study update. (June 2019) Authors: Schultz, M; Swoboda, K; Farrar, M; McMillan, H; Parsons, J; Farrow, M; Ogrinc, FG; Feltner, DE; McGill, BE; Spector, SA; L'Italien, J; Sproule, DM; Strauss, KA Journal: Canadian journal of neurological sciences Issue: Volume 46(2019)Supplement 1 Page Start: S31 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗