1. An open‐label study to determine the pharmacokinetics and safety of migalastat HCl in subjects with impaired renal function and healthy subjects with normal renal function. Issue 4 (22nd December 2014) Authors: Johnson, Franklin K.; Mudd, Paul N.; DiMino, Tara; Vosk, Jennie; Sitaraman, Sheela; Boudes, Pol; France, Nicholas; Barlow, Carrolee Journal: Clinical pharmacology in drug development Issue: Volume 4:Issue 4(2015:Jul./Aug.) Page Start: 256 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
2. An open‐label study to determine the pharmacokinetics and safety of migalastat HCl in subjects with impaired renal function and healthy subjects with normal renal function. Issue 4 (22nd December 2014) Authors: Johnson, Franklin K.; Mudd, Paul N.; DiMino, Tara; Vosk, Jennie; Sitaraman, Sheela; Boudes, Pol; France, Nicholas; Barlow, Carrolee Journal: Clinical pharmacology in drug development Issue: Volume 4:Issue 4(2015:Jul./Aug.) Page Start: 256 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
3. Safety and efficacy of cipaglucosidase alfa plus miglustat versus alglucosidase alfa plus placebo in late-onset Pompe disease (PROPEL): an international, randomised, double-blind, parallel-group, phase 3 trial. Issue 12 (December 2021) Authors: Schoser, Benedikt; Roberts, Mark; Byrne, Barry J; Sitaraman, Sheela; Jiang, Hai; Laforêt, Pascal; Toscano, Antonio; Castelli, Jeff; Díaz-Manera, Jordi; Goldman, Mitchell; van der Ploeg, Ans T; Bratkovic, Drago; Kuchipudi, Srilakshmi; Mozaffar, Tahseen; Kishnani, Priya S; Sebok, Agnes; Pestronk, A... Journal: Lancet neurology Issue: Volume 20:Issue 12(2021) Page Start: 1027 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗