1. Regulatory environment for novel therapeutic development in mitochondrial diseases. Issue 2 (4th January 2021) Authors: Hirano, Michio; Berardo, Andres; Barca, Emanuele; Emmanuele, Valentina; Quinzii, Catarina; Simpson, Camilla V.; Engelstad, Kristin; Rosales, Xiomara Q.; Thompson, John L. P. Journal: Journal of inherited metabolic disease Issue: Volume 44:Issue 2(2021) Page Start: 292 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗