1. S61 Onasemnogene abeparvovec gene-replacement therapy (GRT) for spinal muscular atrophy type 1 (SMA1): preliminary pulmonary and ventilatory findings from the phase 3 study (STR1VE). (12th November 2019) Authors: Shell, R; Day, JW; Chiriboga, CA; Crawford, TO; Darras, BT; Finkel, RS; Connolly, AM; Iannaccone, ST; Kuntz, NL; Peña, LDM; Shieh, PB; Smith, EC; Kausar, I; Schultz, M; Feltner, DE; Ogrinc, FG; Macek, TA; Kernbauer, E; L'Italien, J; Sproule, DM Journal: Thorax Issue: Volume 74(2019)Supplement 2 Page Start: A42 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗