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1. S43. A PROOF-OF-MECHANISM STUDY OF THE PDE10 INHIBITOR RG7203 IN PATIENTS WITH PROBING REWARD FUNCTIONS WITH IMAGING AND BEHAVIORAL APPROACHES. (1st April 2018)

4. Design of a Phase 1/2 study of an AAV9‐based gene therapy for fronto‐temporal dementia patients with pathogenic GRN mutations (PROCLAIM trial): Human/Trial design. (7th December 2020)