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Author/Creator Roper, Helen

1. A Phase 1b Trial to Assess the Pharmacokinetics of Ezutromid in Pediatric Duchenne Muscular Dystrophy Patients on a Balanced Diet. Issue 7 (16th January 2019)

Authors:
Muntoni, Francesco; Tejura, Bina; Spinty, Stefan; Roper, Helen; Hughes, Imelda; Layton, Gary; Davies, Kay E.; Harriman, Shawn; Tinsley, Jonathon
Journal:
Clinical pharmacology in drug development
Issue:
Volume 8:Issue 7(2019)
Page Start:
922
Record Type:
Journal Article
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Available online (eLD content is only available in our Reading Rooms) ↗

5. Randomised placebo-controlled trial of combination ACE inhibitor and beta-blocker therapy to prevent cardiomyopathy in children with Duchenne muscular dystrophy? (DMD Heart Protection Study): a protocol study. Issue 12 (19th December 2018)

Authors:
Bourke, John P; Watson, Gillian; Muntoni, Francesco; Spinty, Stefan; Roper, Helen; Guglieri, Michela; Speed, Chris; McColl, Elaine; Chikermane, Ashish; Jayawant, Sandeep; Adwani, Satish; Willis, Tracey; Wilkinson, Jennifer; Bryant, Andrew; Chadwick, Thomas; Wood, Ruth; Bushby, Kate
Journal:
BMJ open
Issue:
Volume 8:Issue 12(2018)
Page Start:
Record Type:
Journal Article
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Available online (eLD content is only available in our Reading Rooms) ↗

7. TRAPPC11‐related muscular dystrophy with hypoglycosylation of alpha‐dystroglycan in skeletal muscle and brain. (11th November 2021)

Authors:
Munot, Pinki; McCrea, Nadine; Torelli, Silvia; Manzur, Adnan; Sewry, Caroline; Chambers, Darren; Feng, Lucy; Ala, Pierpaolo; Zaharieva, Irina; Ragge, Nicola; Roper, Helen; Marton, Tamas; Cox, Phil; Milev, Miroslav P.; Liang, Wen‐Chen; Maruyama, Shinsuke; Nishino, Ichizo; Sacher, Michael; Phadke, ...
Journal:
Neuropathology & applied neurobiology
Issue:
Volume 48:Number 2(2022)
Page Start:
n/a
Record Type:
Journal Article
View Content:
Available online (eLD content is only available in our Reading Rooms) ↗