1. Treatment of infantile-onset spinal muscular atrophy with nusinersen: final report of a phase 2, open-label, multicentre, dose-escalation study. (July 2021) Authors: Finkel, Richard S; Chiriboga, Claudia A; Vajsar, Jiri; Day, John W; Montes, Jacqueline; De Vivo, Darryl C; Bishop, Kathie M; Foster, Richard; Liu, Yingying; Ramirez-Schrempp, Daniela; Schneider, Eugene; Bennett, C Frank; Wong, Janice; Farwell, Wildon Journal: Lancet Issue: Volume 5:Number 7(2021) Page Start: 491 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗