1. Repeated intravenous cardiosphere-derived cell therapy in late-stage Duchenne muscular dystrophy (HOPE-2): a multicentre, randomised, double-blind, placebo-controlled, phase 2 trial. Issue 10329 (12th March 2022) Authors: McDonald, Craig M; Marbán, Eduardo; Hendrix, Suzanne; Hogan, Nathaniel; Ruckdeschel Smith, Rachel; Eagle, Michelle; Finkel, Richard S; Tian, Cuixia; Janas, Joanne; Harmelink, Matthew M; Varadhachary, Arun S; Taylor, Michael D; Hor, Kan N; Mayer, Oscar H; Henricson, Erik K; Furlong, Pat; Ascheim, ... Journal: Lancet Issue: Volume 399:Issue 10329(2022) Page Start: 1049 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
2. Siblings With Mutations in TRAPPC11 Presenting With Limb-Girdle Muscular Dystrophy 2S. Issue 1 (September 2017) Authors: Fee, Dominic B.; Harmelink, Matthew; Monrad, Priya; Pyzik, Erika Journal: Journal of clinical neuromuscular disease Issue: Volume 19:Issue 1(2017:Sep.) Page Start: Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗