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Author/Creator Phillips, Dawn

1. Asfotase alfa for infants and young children with hypophosphatasia: 7 year outcomes of a single-arm, open-label, phase 2 extension trial. Issue 2 (February 2019)

Authors:
Whyte, Michael P; Simmons, Jill H; Moseley, Scott; Fujita, Kenji P; Bishop, Nicholas; Salman, Nada J; Taylor, John; Phillips, Dawn; McGinn, Mairead; McAlister, William H
Journal:
Lancet
Issue:
Volume 7:Issue 2(2019)
Page Start:
93
Record Type:
Journal Article
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2. Comprehensive long‐term efficacy and safety of recombinant human alpha‐mannosidase (velmanase alfa) treatment in patients with alpha‐mannosidosis. Issue 6 (3rd May 2018)

Authors:
Lund, Allan M.; Borgwardt, Line; Cattaneo, Federica; Ardigò, Diego; Geraci, Silvia; Gil‐Campos, Mercedes; De Meirleir, Linda; Laroche, Cécile; Dolhem, Philippe; Cole, Duncan; Tylki‐Szymanska, Anna; Lopez‐Rodriguez, Monica; Guillén‐Navarro, Encarna; Dali, Christine I.; Héron, Bénédicte; Fogh, Jens...
Journal:
Journal of inherited metabolic disease
Issue:
Volume 41:Issue 6(2018)
Page Start:
1225
Record Type:
Journal Article
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3. Health Related Quality of Life, Disability, and Pain in Alpha Mannosidosis: Long-Term Data of Enzyme Replacement Therapy With Velmanase Alfa (Human Recombinant Alpha Mannosidase). (3rd September 2018)

Authors:
Borgwardt, Line; Guffon, Nathalie; Amraoui, Yasmina; Jones, Simon A.; De Meirleir, Linda; Lund, Allan M.; Gil-Campos, Mercedes; Van den Hout, Johanna M. P.; Tylki-Szymanska, Anna; Geraci, Silvia; Ardigò, Diego; Cattaneo, Federica; Harmatz, Paul; Phillips, Dawn
Journal:
Journal of inborn errors of metabolism and screening
Issue:
Volume 6(2018)
Page Start:
Record Type:
Journal Article
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