1. J06 Pivot-HD: a phase 2, randomised, placebo-controlled study to evaluate the safety and efficacy of ptc518 in subjects with Huntington's disease. (12th September 2022) Authors: Beers, Brian; Bredlau, Amy-Lee; Bhattacharyya, Anu; Kristensen, Allan; Golden, Lee; Klein, Matthew; Peltz, Stuart Journal: Journal of neurology, neurosurgery and psychiatry Issue: Volume 93(2022)Supplement 1 Page Start: A96 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
2. THE 6‐minute walk test and other endpoints in Duchenne muscular dystrophy: Longitudinal natural history observations over 48 weeks from a multicenter study. Issue 3 (26th June 2013) Authors: Mcdonald, Craig M.; Henricson, Erik K.; Abresch, R. Ted; Florence, Julaine M.; Eagle, Michelle; Gappmaier, Eduard; Glanzman, Allan M.; Spiegel, Robert; Barth, Jay; Elfring, Gary; Reha, Allen; Peltz, Stuart Journal: Muscle & nerve Issue: Volume 48:Issue 3(2013:Sep.) Page Start: 343 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗