1. Long-term Safety and Efficacy of Avalglucosidase Alfa in Patients With Late-Onset Pompe Disease. (2nd August 2022) Authors: Dimachkie, Mazen M.; Barohn, Richard J.; Byrne, Barry; Goker-Alpan, Ozlem; Kishnani, Priya S.; Ladha, Shafeeq; Laforêt, Pascal; Mengel, Karl Eugen; Peña, Loren D.M.; Sacconi, Sabrina; Straub, Volker; Trivedi, Jaya; Van Damme, Philip; van der Ploeg, Ans T.; Vissing, John; Young, Peter; Haack, Kris... Journal: Neurology Issue: Volume 99:Number 5(2022) Page Start: e536 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗