1. Gene Therapy Getting Personal: Mutation-Specific Editing and Gene Addition Strategies for β-Thalassaemia. (2nd November 2019) Authors: Lederer, Carsten W.; Patsali, Petros; Mussolino, Claudio; Turchiano, Giandomenico; Papasavva, Panayiota; Romito, Marianna; Stephanou, Coralea; Cornu, Tatjana I.; Kolnagou, Annita; Christou, Soteroula; Sitarou, Maria; Antoniou, Mike N.; Cathomen, Toni; Kleanthous, Marina Journal: Hemoglobin Issue: Volume 43:Number 6(2019) Page Start: 330 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗