1. Antisense oligonucleotides correct the familial dysautonomia splicing defect in IKBKAP transgenic mice. Issue 10 (17th April 2018) Authors: Sinha, Rahul; Kim, Young Jin; Nomakuchi, Tomoki; Sahashi, Kentaro; Hua, Yimin; Rigo, Frank; Bennett, C Frank; Krainer, Adrian R Journal: Nucleic acids research Issue: Volume 46:Issue 10(2018) Page Start: 4833 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
2. Pathological impact of SMN2 mis‐splicing in adult SMA mice. Issue 10 (9th September 2013) Authors: Sahashi, Kentaro; Ling, Karen K. Y.; Hua, Yimin; Wilkinson, John Erby; Nomakuchi, Tomoki; Rigo, Frank; Hung, Gene; Xu, David; Jiang, Ya‐Ping; Lin, Richard Z.; Ko, Chien‐Ping; Bennett, C. Frank; Krainer, Adrian R. Journal: EMBO molecular medicine Issue: Volume 5:Issue 10(2013:Oct.) Page Start: 1586 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗