1. ATTRv amyloidosis Italian Registry: clinical and epidemiological data. (1st October 2020) Authors: Russo, Massimo; Obici, Laura; Bartolomei, Ilaria; Cappelli, Francesco; Luigetti, Marco; Fenu, Silvia; Cavallaro, Tiziana; Chiappini, Maria Grazia; Gemelli, Chiara; Pradotto, Luca Guglielmo; Manganelli, Fiore; Leonardi, Luca; My, Filomena; Sampaolo, Simone; Briani, Chiara; Gentile, Luca; Stancanel... Journal: Amyloid Issue: Volume 27:Number 4(2020) Page Start: 259 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
2. Real‐life experience with inotersen in hereditary transthyretin amyloidosis with late‐onset phenotype: Data from an early‐access program in Italy. (28th March 2022) Authors: Luigetti, Marco; Antonini, Giovanni; Di Paolantonio, Andrea; Gentile, Luca; Grandis, Marina; Leonardi, Luca; Lozza, Alessandro; Manganelli, Fiore; Mazzeo, Anna; Mussinelli, Roberta; My, Filomena; Obici, Laura; Maria Pennisi, Elena; Romozzi, Marina; Russo, Massimo; Sabatelli, Mario; Salvalagg... Journal: European journal of neurology Issue: Volume 29:Number 7(2022) Page Start: 2148 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗