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Author/Creator Morando, S.

3. Onasemnogene abeparvovec gene therapy for symptomatic infantile-onset spinal muscular atrophy type 1 (STR1VE-EU): an open-label, single-arm, multicentre, phase 3 trial. Issue 10 (October 2021)

Authors:
Mercuri, Eugenio; Muntoni, Francesco; Baranello, Giovanni; Masson, Riccardo; Boespflug-Tanguy, Odile; Bruno, Claudio; Corti, Stefania; Daron, Aurore; Deconinck, Nicolas; Servais, Laurent; Straub, Volker; Ouyang, Haojun; Chand, Deepa; Tauscher-Wisniewski, Sitra; Mendonca, Nuno; Lavrov, Arseniy; Se...
Journal:
Lancet neurology
Issue:
Volume 20:Issue 10(2021)
Page Start:
832
Record Type:
Journal Article
View Content:
Available online (eLD content is only available in our Reading Rooms) ↗

5. Sometimes they come back: New and old spinal muscular atrophy adults in the era of nusinersen. (31st October 2020)

Authors:
Sansone, V. A.; Coratti, G.; Pera, M. C.; Pane, M.; Messina, S.; Salmin, F.; Albamonte, E.; De Sanctis, R.; Sframeli, M.; Di Bella, V.; Morando, S.; d'Amico, A.; Frongia, A. L.; Antonaci, L.; Pirola, A.; Pedemonte, M.; Bertini, E.; Bruno, C.; Mercuri, E.
Other Names:
Di Bari Alessandra investigator.; Signorino Amelia investigator.; Longo Antonella investigator.; Tacchetti Paola investigator.; Brolatti Noemi investigator.; Rossi Diletta investigator.; Bravetti Chiara investigator.; Lucibello Simona investigator.; Fanelli Lavinia investigator.; Forcina Nicola i...
Journal:
European journal of neurology
Issue:
Volume 28:Number 2(2021)
Page Start:
602
Record Type:
Journal Article
View Content:
Available online (eLD content is only available in our Reading Rooms) ↗