1. Efficacy and safety of givosiran for acute hepatic porphyria: 24‐month interim analysis of the randomized phase 3 ENVISION study. (16th November 2021) Authors: Ventura, Paolo; Bonkovsky, Herbert L.; Gouya, Laurent; Aguilera‐Peiró, Paula; Montgomery Bissell, D.; Stein, Penelope E.; Balwani, Manisha; Anderson, D. Karl E.; Parker, Charles; Kuter, David J.; Monroy, Susana; Oh, Jeeyoung; Ritchie, Bruce; Ko, John J.; Hua, Zhaowei; Sweetser, Marianne T.; Sardh... Journal: Liver international Issue: Volume 42:Number 1(2022) Page Start: 161 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
2. EXPLORE B: A prospective, long‐term natural history study of patients with acute hepatic porphyria with chronic symptoms. Issue 6 (18th September 2022) Authors: Cassiman, David; Kauppinen, Raili; Monroy, Susana; Lee, Ming‐Jen; Bonkovsky, Herbert L.; Thapar, Manish; Guillén‐Navarro, Encarna; Minder, Anna‐Elisabeth; Hale, Cecilia; Sweetser, Marianne T.; Ivanova, Aneta Journal: Journal of inherited metabolic disease Issue: Volume 45:Issue 6(2022) Page Start: 1163 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
3. Inside Front Cover. (19th January 2022) Authors: Ventura, Paolo; Bonkovsky, Herbert L.; Gouya, Laurent; Aguilera‐Peiró, Paula; Montgomery Bissell, D.; Stein, Penelope E.; Balwani, Manisha; Anderson, D. Karl E.; Parker, Charles; Kuter, David J.; Monroy, Susana; Oh, Jeeyoung; Ritchie, Bruce; Ko, John J.; Hua, Zhaowei; Sweetser, Marianne T.; Sardh... Journal: Liver international Issue: Volume 42:Number 1(2022) Page Start: ii Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
4. Issue Cover. (29th December 2021) Authors: Ventura, Paolo; Bonkovsky, Herbert L.; Gouya, Laurent; Aguilera‐Peiró, Paula; Montgomery Bissell, D.; Stein, Penelope E.; Balwani, Manisha; Anderson, D. Karl E.; Parker, Charles; Kuter, David J.; Monroy, Susana; Oh, Jeeyoung; Ritchie, Bruce; Ko, John J.; Hua, Zhaowei; Sweetser, Marianne T.; Sardh... Journal: Liver international Issue: Volume 42:Number 1(2022) Page Start: i Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
5. S1169 Twelve-Month Interim Analysis of Efficacy and Safety of Givosiran, an Investigational RNAi Therapeutic for Acute Hepatic Porphyria, in the ENVISION Open Label Extension. (October 2020) Authors: Sardh, Eliane; Balwani, Manisha; Rees, David C.; Stein, Penelope; Stölzel, Ulrich; Peiro, Paula Aguilera; Bissell, D. Montgomery; Bonkovsky, Herbert L.; Keel, Sioban; Parker, Charles; Phillips, John D.; Silver, Samuel; Windyga, Jerzy; D'Avola, Delia; Ross, Gayle; Stewart, Peter; Ritchie, Bruce; H... Journal: American journal of gastroenterology Issue: Volume 115:Supplement(2020)ACG Annual Meeting Abstracts 1 Page Start: S584 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
6. S1170 Efficacy and Safety of Givosiran in Patients With Acute Hepatic Porphyria: 24-Month Interim Analysis of the Phase 3 ENVISION Randomized Clinical Trial. (October 2021) Authors: Bonkovsky, Herbert L.; Ventura, Paolo; Gouya, Laurent; Peiró, Paula Aguilera; Bissell, D. Montgomery; Stein, Penelope E.; Anderson, Karl E.; Monroy, Susana; Kuter, David J.; Oh, Jeeyoung; Ko, John J.; Hua, Zhaowei; Sweetser, Marianne T.; Sardh, Eliane Journal: American journal of gastroenterology Issue: Volume 116:Supplement(2021)ACG Annual Meeting Abstracts 1 Page Start: S545 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
7. S1171 EXPLORE Part B: A Prospective, International, Long-Term Natural History Study of Patients With Acute Hepatic Porphyria With Recurrent Symptoms. (October 2021) Authors: Cassiman, David M.; Kauppinen, Raili M.; Monroy, Susana; Lee, Ming-Jen; Bonkovsky, Herbert L.; FACG, ; Thapar, Manish; Guillén-Navarro, Encarna; Hua, Zhaowei; Sweetser, Marianne T.; Ivanova, Aneta V. Journal: American journal of gastroenterology Issue: Volume 116:Supplement(2021)ACG Annual Meeting Abstracts 1 Page Start: S546 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗