1. A phase 3 clinical trial with ISIS-TTRRx, a 2nd-generation antisense oligonucleotide targeting transthyretin (TTR), for the treatment of TTR amyloid cardiomyopathy. Issue 1 (December 2015) Authors: Millns, Helen; Bergemann, Rito; Ackermann, Elizabeth; Monia, Brett; Lukas, Mary Journal: Orphanet journal of rare diseases Issue: Volume 9:Issue 1(2014) Page Start: 1 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
2. Antisense therapy targeting complement factor B. (October 2018) Authors: Grossman, Tamar; Carrer, Michele; Johnson, Robert; Shen, Lijiang; Hettrick, Lisa; Henry, Scott; Monia, Brett; McCaleb, Michael Journal: Molecular immunology Issue: Volume 102(2018:Oct.) Page Start: 156 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
3. Pharmacodynamic efficacy of IONIS-FB-LRX, a complement factor B antisense oligonucleotide, in a phase 1 clinical study. (October 2018) Authors: McCaleb, Michael; Hughes, Steve; Greary, Richard; Monia, Brett; Grossman, Tamar Journal: Molecular immunology Issue: Volume 102(2018:Oct.) Page Start: 187 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
4. Population pharmacokinetic/pharmacodynamic modelling of eplontersen, an antisense oligonucleotide in development for transthyretin amyloidosis. Issue 12 (7th August 2022) Authors: Diep, John K.; Yu, Rosie Z.; Viney, Nicholas J.; Schneider, Eugene; Guo, Shuling; Henry, Scott; Monia, Brett; Geary, Richard; Wang, Yanfeng Other Names: Wong Ian guestEditor.; Dewildt Saskia guestEditor. Journal: British journal of clinical pharmacology Issue: Volume 88:Issue 12(2022) Page Start: 5389 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
5. The ISIS-TTRRx-CS2 phase 3 study in patients with familial amyloid polyneuropathy: Baseline results of the first 100 patients for the NIS, NIS+7 and mNIS+7 using different methods of scoring: identification of consistencies and key differences. Issue 1 (December 2015) Authors: Bergemann, Rito; Ackermann, Elizabeth; Monia, Brett; Shenker, Andrew; Dyck, Peter Journal: Orphanet journal of rare diseases Issue: Volume 9:Issue 1(2014) Page Start: 1 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗