1. Disease Characteristics of Acute Hepatic Porphyria Patients: ENVISION, a Phase 3 Global, Multicenter, Randomized, Double‐Blind, Placebo‐Controlled Trial: 996. (October 2019) Authors: Anderson, Karl; Balwani, Manisha; Sardh, Eliane; Gouya, Laurent; Rees, David; Stein, Penelope; Stolzel, Ulrich; Aguilera, Paula; Bissell, Montgomery D.; Bonkovsky, Herbert; Keel, Sioban; Parker, Charles; Phillips, John; Silver, Samuel; Windyga, Jerzy; D'Avola, Delia; Ross, Gayle; Stewart, Peter; ... Journal: American journal of gastroenterology Issue: Volume 114 (2019)ACG Abstracts 1:Supplement Page Start: Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
2. EXPLORE: A Prospective, Multinational, Natural History Study of Patients with Acute Hepatic Porphyria with Recurrent Attacks. Issue 5 (7th November 2019) Authors: Gouya, Laurent; Ventura, Paolo; Balwani, Manisha; Bissell, D. Montgomery; Rees, David C.; Stölzel, Ulrich; Phillips, John D.; Kauppinen, Raili; Langendonk, Janneke G.; Desnick, Robert J.; Deybach, Jean‐Charles; Bonkovsky, Herbert L.; Parker, Charles; Naik, Hetanshi; Badminton, Michael; Stein, Pen... Journal: Hepatology Issue: Volume 71:Issue 5(2020) Page Start: 1546 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
3. S1154 Clinical Outcomes in Patients With Acute Hepatic Porphyria Treated With Givosiran Who Stopped Hemin Prophylaxis at Study Entry: A Post Hoc Analysis of Data From the Phase 3 ENVISION Study Through Month 12. (October 2020) Authors: Bonkovsky, Herbert L.; Balwani, Manisha; Sardh, Eliane; Gouya, Laurent; Rees, David C.; Stein, Penelope; Stölzel, Ulrich; Peiro, Paula Aguilera; Bissell, D. Montgomery; Keel, Sioban; Parker, Charles; Silver, Samuel; Windyga, Jerzy; D'Avola, Delia; Ross, Gayle; Stewart, Peter; Ritchie, Bruce; Oh, ... Journal: American journal of gastroenterology Issue: Volume 115:Supplement(2020)ACG Annual Meeting Abstracts 1 Page Start: S578 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗