1. 130 Safety, β-sarcoglycan expression and functional outcomes from systemic gene transfer of rAAVrh74.MHCK7.SGCB in LGMD2E/R4. Issue 6 (27th May 2022) Authors: Rodino-Klapac, Louise; Pozsgai, Eric; Lewis, Sarah; Griffin, Danielle; Meadows, Aaron; Lehman, Kelly; Church, Kathleen; Lowes, Linda; Richardson, James; Mendell, Jerry Journal: Journal of neurology, neurosurgery and psychiatry Issue: Volume 93:Issue 6(2022) Page Start: A141 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
2. 260 Gene transfer with rAAVrh74.MHCK7.SGCB increased β-sarcoglycan expression in LGMD type 2E patients. Issue 6 (27th May 2022) Authors: Richardson, James; Rodino-Klapac, Louise; Pozsgai, Eric; Lewis, Sarah; Griffin, Danielle; Lehman, Kelly; Church, Kathleen; Miller, Natalie; Iammarino, Megan; Lowes, Linda; Mendell, Jerry Journal: Journal of neurology, neurosurgery and psychiatry Issue: Volume 93:Issue 6(2022) Page Start: A88 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
3. Reducing sarcolipin expression mitigates Duchenne muscular dystrophy and associated cardiomyopathy in mice. Issue 1 (December 2017) Authors: Voit, Antanina; Patel, Vishwendra; Pachon, Ronald; Shah, Vikas; Bakhutma, Mohammad; Kohlbrenner, Erik; McArdle, Joseph J.; Dell'Italia, Louis; Mendell, Jerry; Xie, Lai-Hua; Hajjar, Roger; Duan, Dongsheng; Fraidenraich, Diego; Babu, Gopal Journal: Nature communications Issue: Volume 8:Issue 1(2017) Page Start: 1 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗