1. Ataluren in patients with nonsense mutation Duchenne muscular dystrophy (ACT DMD): a multicentre, randomised, double-blind, placebo-controlled, phase 3 trial. Issue 10101 (23rd September 2017) Authors: McDonald, Craig M; Campbell, Craig; Torricelli, Ricardo Erazo; Finkel, Richard S; Flanigan, Kevin M; Goemans, Nathalie; Heydemann, Peter; Kaminska, Anna; Kirschner, Janbernd; Muntoni, Francesco; Osorio, Andrés Nascimento; Schara, Ulrike; Sejersen, Thomas; Shieh, Perry B; Sweeney, H Lee; Topaloglu... Journal: Lancet Issue: Volume 390:Issue 10101(2017) Page Start: 1489 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
2. Efficacy of idebenone on respiratory function in patients with Duchenne muscular dystrophy not using glucocorticoids (DELOS): a double-blind randomised placebo-controlled phase 3 trial. Issue 9979 (2nd May 2015) Authors: Buyse, Gunnar M; Voit, Thomas; Schara, Ulrike; Straathof, Chiara S M; D'Angelo, M Grazia; Bernert, Günther; Cuisset, Jean-Marie; Finkel, Richard S; Goemans, Nathalie; McDonald, Craig M; Rummey, Christian; Meier, Thomas Journal: Lancet Issue: Volume 385:Issue 9979(2015) Page Start: 1748 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
3. Evidence-based care in Duchenne muscular dystrophy. Issue 5 (May 2018) Authors: McDonald, Craig M; Mercuri, Eugenio Journal: Lancet neurology Issue: Volume 17:Issue 5(2018) Page Start: 389 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
4. Influence of β1 Adrenergic Receptor Genotype on Longitudinal Measures of Left Ventricular Ejection Fraction and Responsiveness to ß-Blocker Therapy in Patients With Duchenne Muscular Dystrophy. Issue 16 (August 2022) Authors: Kelley, Eli F; Cross, Troy J; McDonald, Craig M; Investigators, CINRG; Hoffman, Eric P; Spurney, Christopher F; Bello, Luca Journal: Clinical Medicine Insights Issue: Issue 16(2022) Page Start: Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
5. Long-term effects of glucocorticoids on function, quality of life, and survival in patients with Duchenne muscular dystrophy: a prospective cohort study. Issue 10119 (3rd February 2018) Authors: McDonald, Craig M; Henricson, Erik K; Abresch, Richard T; Duong, Tina; Joyce, Nanette C; Hu, Fengming; Clemens, Paula R; Hoffman, Eric P; Cnaan, Avital; Gordish-Dressman, Heather; Vishwanathan, Vijay; Chidambaranathan, S; Biggar, W. Douglas; McAdam, Laura C.; Mah, Jean K.; Tulinius, Mar; Cnaan, A... Journal: Lancet Issue: Volume 391:Issue 10119(2018) Page Start: 451 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
6. Long-term effects of glucocorticoids on function, quality of life, and survival in patients with Duchenne muscular dystrophy: a prospective cohort study. Issue 10119 (3rd February 2018) Authors: McDonald, Craig M; Henricson, Erik K; Abresch, Richard T; Duong, Tina; Joyce, Nanette C; Hu, Fengming; Clemens, Paula R; Hoffman, Eric P; Cnaan, Avital; Gordish-Dressman, Heather Journal: Lancet Issue: Volume 391:Issue 10119(2018) Page Start: 451 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
7. Neuromuscular disease management and rehabilitation. (2012) Other Names: Joyce, Nanette C; McDonald, Craig M Record Type: Book Extent: 1 online resource (240 pages) View Content: Available online (eLD content is only available in our Reading Rooms) ↗
8. Neuromuscular disease management and rehabilitation. specialty care and therapeutics /: specialty care and therapeutics. Part II : (©2012) Other Names: Joyce, Nanette C; McDonald, Craig M Record Type: Book Extent: 1 online resource, illustrations (some color) View Content: Available online (eLD content is only available in our Reading Rooms) ↗
9. Repeated intravenous cardiosphere-derived cell therapy in late-stage Duchenne muscular dystrophy (HOPE-2): a multicentre, randomised, double-blind, placebo-controlled, phase 2 trial. Issue 10329 (12th March 2022) Authors: McDonald, Craig M; Marbán, Eduardo; Hendrix, Suzanne; Hogan, Nathaniel; Ruckdeschel Smith, Rachel; Eagle, Michelle; Finkel, Richard S; Tian, Cuixia; Janas, Joanne; Harmelink, Matthew M; Varadhachary, Arun S; Taylor, Michael D; Hor, Kan N; Mayer, Oscar H; Henricson, Erik K; Furlong, Pat; Ascheim, ... Journal: Lancet Issue: Volume 399:Issue 10329(2022) Page Start: 1049 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗