1. An innovative hematopoietic stem cell gene therapy approach benefits CLN1 disease in the mouse model. Issue 4 (6th March 2023) Authors: Peviani, Marco; Das, Sabyasachi; Patel, Janki; Jno‐Charles, Odella; Kumar, Rajesh; Zguro, Ana; Mathews, Tyler D; Cabras, Paolo; Milazzo, Rita; Cavalca, Eleonora; Poletti, Valentina; Biffi, Alessandra Journal: EMBO molecular medicine Issue: Volume 15:Issue 4(2023) Page Start: n/a Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗