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Author/Creator Jaber, Birgit

2. A phase 1 healthy male volunteer single escalating dose study of the pharmacokinetics and pharmacodynamics of risdiplam (RG7916, RO7034067), a SMN2 splicing modifier. Issue 1 (16th November 2018)

Authors:
Sturm, Stefan; Günther, Andreas; Jaber, Birgit; Jordan, Paul; Al Kotbi, Nada; Parkar, Nikhat; Cleary, Yumi; Frances, Nicolas; Bergauer, Tobias; Heinig, Katja; Kletzl, Heidemarie; Marquet, Anne; Ratni, Hasane; Poirier, Agnès; Müller, Lutz; Czech, Christian; Khwaja, Omar
Journal:
British journal of clinical pharmacology
Issue:
Volume 85:Issue 1(2019)
Page Start:
181
Record Type:
Journal Article
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Available online (eLD content is only available in our Reading Rooms) ↗

4. Risdiplam treatment has not led to retinal toxicity in patients with spinal muscular atrophy. Issue 1 (24th November 2020)

Authors:
Sergott, Robert C.; Amorelli, Giulia M.; Baranello, Giovanni; Barreau, Emmanuel; Beres, Shannon; Kane, Steven; Mercuri, Eugenio; Orazi, Lorenzo; SantaMaria, Melissa; Tremolada, Gemma; Santarsiero, Diletta; Waskowska, Agnieszka; Yashiro, Shigeko; Denk, Nora; Fürst‐Recktenwald, Sabine; Gerber, Mari...
Journal:
Annals of clinical and translational neurology
Issue:
Volume 8:Issue 1(2021)
Page Start:
54
Record Type:
Journal Article
View Content:
Available online (eLD content is only available in our Reading Rooms) ↗

5. Risdiplam treatment has not led to retinal toxicity in patients with spinal muscular atrophy. Issue 1 (24th November 2020)

Authors:
Sergott, Robert C.; Amorelli, Giulia M.; Baranello, Giovanni; Barreau, Emmanuel; Beres, Shannon; Kane, Steven; Mercuri, Eugenio; Orazi, Lorenzo; SantaMaria, Melissa; Tremolada, Gemma; Santarsiero, Diletta; Waskowska, Agnieszka; Yashiro, Shigeko; Denk, Nora; Fürst‐Recktenwald, Sabine; Gerber, Mari...
Journal:
Annals of clinical and translational neurology
Issue:
Volume 8:Issue 1(2021)
Page Start:
54
Record Type:
Journal Article
View Content:
Available online (eLD content is only available in our Reading Rooms) ↗

6. Safety and efficacy of risdiplam in patients with type 1 spinal muscular atrophy (FIREFISH part 2): secondary analyses from an open-label trial. Issue 12 (December 2022)

Authors:
Masson, Riccardo; Mazurkiewicz-Bełdzińska, Maria; Rose, Kristy; Servais, Laurent; Xiong, Hui; Zanoteli, Edmar; Baranello, Giovanni; Bruno, Claudio; Day, John W; Deconinck, Nicolas; Klein, Andrea; Mercuri, Eugenio; Vlodavets, Dmitry; Wang, Yi; Dodman, Angela; El-Khairi, Muna; Gorni, Ksenija; Jaber...
Journal:
Lancet neurology
Issue:
Volume 21:Issue 12(2022)
Page Start:
1110
Record Type:
Journal Article
View Content:
Available online (eLD content is only available in our Reading Rooms) ↗