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You searched for: Author/Creator Ismail, Hesham M.- Ismail, Hesham M. [remove] 2
- 615.1 1
- 616.04205 1
- CBS -- chemical chaperones -- Homocystinuria -- in silico -- in vivo models -- p.R336C mutation -- Qatar 1
- Chemotherapy -- Periodicals 1
- Duchenne muscular dystrophy -- socioeconomic impact -- drug price -- drug repurposing -- orphan drug designation 1
- Human chromosome abnormalities -- Periodicals 1
- Mutation (Biology) -- Periodicals 1
- Orphan drugs -- Periodicals 1
- Rare diseases -- Periodicals 1