1. Long‐term efficacy of miglustat in paediatric patients with Niemann‐Pick disease type C. Issue 1 (5th April 2012) Authors: Chien, Y. H.; Peng, S. F.; Yang, C. C.; Lee, N. C.; Tsai, L. K.; Huang, A. C.; Su, S. C.; Tseng, C. C.; Hwu, W. L. Journal: Journal of inherited metabolic disease Issue: Volume 36:Issue 1(2013) Page Start: 129 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗