1. Antisense suppression of glial fibrillary acidic protein as a treatment for Alexander disease. Issue 1 (14th January 2018) Authors: Hagemann, Tracy L.; Powers, Berit; Mazur, Curt; Kim, Aneeza; Wheeler, Steven; Hung, Gene; Swayze, Eric; Messing, Albee Journal: Annals of neurology Issue: Volume 83:Issue 1(2018) Page Start: 27 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
2. Pathological impact of SMN2 mis‐splicing in adult SMA mice. Issue 10 (9th September 2013) Authors: Sahashi, Kentaro; Ling, Karen K. Y.; Hua, Yimin; Wilkinson, John Erby; Nomakuchi, Tomoki; Rigo, Frank; Hung, Gene; Xu, David; Jiang, Ya‐Ping; Lin, Richard Z.; Ko, Chien‐Ping; Bennett, C. Frank; Krainer, Adrian R. Journal: EMBO molecular medicine Issue: Volume 5:Issue 10(2013:Oct.) Page Start: 1586 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
3. Treatment of infantile-onset spinal muscular atrophy with nusinersen: a phase 2, open-label, dose-escalation study. Issue 10063 (17th December 2016) Authors: Finkel, Richard S; Chiriboga, Claudia A; Vajsar, Jiri; Day, John W; Montes, Jacqueline; De Vivo, Darryl C; Yamashita, Mason; Rigo, Frank; Hung, Gene; Schneider, Eugene; Norris, Daniel A; Xia, Shuting; Bennett, C Frank; Bishop, Kathie M Journal: Lancet Issue: Volume 388:Issue 10063(2016) Page Start: 3017 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗