1. Haematological effects of oral administration of bitopertin, a glycine transport inhibitor, in patients with non‐transfusion‐dependent β‐thalassaemia. (30th April 2021) Authors: Taher, Ali T.; Viprakasit, Vip; Cappellini, Maria Domenica; Kraus, Dominik; Cech, Patrick; Volz, Dietmar; Winter, Erica; Nave, Stephane; Dukart, Juergen; Khwaja, Omar; Koerner, Annette; Hermosilla, Ricardo; Brugnara, Carlo Journal: British journal of haematology Issue: Volume 194:Number 2(2021) Page Start: 474 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
2. Natural history of Type 2 and 3 spinal muscular atrophy: 2‐year NatHis‐SMA study. Issue 2 (24th December 2020) Authors: Annoussamy, Mélanie; Seferian, Andreea M.; Daron, Aurore; Péréon, Yann; Cances, Claude; Vuillerot, Carole; De Waele, Liesbeth; Laugel, Vincent; Schara, Ulrike; Gidaro, Teresa; Lilien, Charlotte; Hogrel, Jean‐Yves; Carlier, Pierre; Fournier, Emmanuel; Lowes, Linda; Gorni, Ksenija; Ly‐Le Moal, Myri... Journal: Annals of clinical and translational neurology Issue: Volume 8:Issue 2(2021) Page Start: 359 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗